Hybrid | 9- 4pm EST
NINDS is a member of the Muscular Dystrophy Coordinating Committee (MDCC), a Federal Advisory Committee including NIH institutes, other Federal agencies, and patient advocates. The MDCC identifies the many challenges confronting people with muscular dystrophy and their families and coordinates efforts to address them.
Agenda
Time | Presentation |
---|---|
9:00 – 9:15 |
Introductions and Meeting Information |
9:15 – 9:35 |
Chair Presentation |
9:35 – 9:45 |
Group Discussion |
9:45 – 10:05 |
New member nominee presentation |
10:05 – 10:50 |
Meeting/Conference Reports FSHD Society International Research Congress 2023 Myotonic Dystrophy Foundation Annual Conference |
10:50 – 11:00 | Break |
11:00 – 12:00 |
Meetings/Conference Reports (continued) AAV tox workshop update Myotonic Dystrophy Young Investigator Conference Limb-Girdle Muscular Dystrophy International Conference Parent Project Muscular Dystrophy Annual Conference and Specialty Meetings |
12:00 - 12:40 |
Recent Advances in Duchenne Muscular Dystrophy Session Introduction DMD Gene Therapy Trial Experience Group discussion |
12:40 – 1:15 | Lunch break |
1:15 – 2:35 |
Recent Advances in Duchenne Muscular Dystrophy (session continued) Progress on Newborn Screening for DMD Clinical Trial Simulation Tool for DMD C-Path's Duchenne Regulatory Science Consortium: Data-Driven Solutions to Enhance Drug Development Session Summary Group Discussion |
2:35 - 2:45 | Break |
2:45 – 3:30 |
Advocacy Group Strategic Plans (Continuation from the Spring 2023 MDCC meeting) Muscular Dystrophy Association Parent Project Muscular Dystrophy |
3:30 – 3:45 |
Update on Renewal of the MDCC Action Plan Group Discussion on Strategic Planning |
3:45 – 4:00 | |
4:00 | Adjourn |